The new gene therapies for sickle cell disease—including the gene-editing treatment Casgevy, based on research at Boston Children's Hospital—have been game-changing for the patients who have ...

Sickle cell anaemia is a genetic blood disorder characterised by the production of an abnormal haemoglobin, known as haemoglobin S. Sickle cell disease changes the shape of blood cells into a crescent ...

Columnist Mary Shaniqua explains how to be an ally to the sickle cell community, and why that kind of support is essential ...

There will be a blood drive for sickle cell disease – the most common inherited blood disorder – this weekend in South Jersey ...

Members of the Indiana General Assembly are calling for more funding for sickle cell disease, including expanding the ...

A new gene editing treatment has been approved for use in the NHS, which will help treat sickle cell disease patients ...

But the results we do have suggest this type of treatment is potentially a cure for sickle cell. Whilst thousands are living with the disease, it won’t be widely available from the start.

This article is part of a Health Affairs Forefront series on “The Future of Sickle Cell Disease Research and Care” with support from The American Society of Hematology. The articles in the ...

Exagamglogene autotemcel (exa-cel) gene therapy offers a potential cure for severe sickle cell disease, now available on NHS.

providing a potential cure for some people with severe sickle cell disease (SCD). It will be made available under a managed access scheme for some people 12 years and over with certain types of severe ...

A sickle cell disease “cure” is to be offered to NHS patients for the first time. The £1.65 million gene therapy called exa-cel, also known under the brand name Casgevy, uses a Nobel Prize ...