GEN3h
Healx Candidate, SpringWorks Therapy Expand NF1 Treatment Options
Healx has dosed the first patient in a Phase II trial assessing its lead pipeline candidate HLX-1502 in patients with neurofibromatosis type 1 (NF1), while the FDA approved SpringWorks Therapeutics’ ...
Gene therapy can improve vision in young children with AIPL1-associated retinal dystrophy
Researchers from the NIHR Moorfields Biomedical Research Centre and University College London have found that gene therapy improved visual acuity and preserved retinal structure in young children with ...
News Medical7h
Researchers challenge previous understanding of tumor growth in NF-1
Despite what was previously thought, new research has shown that genetic changes alone cannot explain why and where tumors grow in those with genetic condition neurofibromatosis type 1 (NF-1).
Genetic study challenges understanding of cancer predisposition
Despite what was previously thought, new research has shown that genetic changes alone cannot explain why and where tumors ...
Hosted on MSN10h
Your guide to AMD - spotlighting the eye condition for February's Awareness Month
Age-Related Macular Degeneration (AMD) is the biggest cause of sight loss in the UK, affecting around 700,000 people. As ...