Bluebird Bio will sell itself to private equity firms Carlyle and SK Capital for about $30 million, the company said Friday.

GMA Network deeply values creativity and regards employees as its greatest assets. We continuously encourage our fellow ...

The company is preparing for two additional commercial launches, with potential approval and launch of Pyrukynd in ...

ACTIVATE-Kids is the First Study to Demonstrate Efficacy of an Oral Therapy for Children with PK Deficiency Who Are Not Regularly Transfused –– ...

Our PYRUKYND franchise is poised for multi-billion-dollar potential, driven by the key milestones we achieved last year, including filing for regulatory approval in thalassemia across four markets and ...

A federal judge on Tuesday ordered government agencies to restore public access to health-related webpages and datasets that ...

Elon Musk is calling for the impeachment of the federal judge who made a decision early Saturday morning that the Treasury ...

After a decade of relying on blood transfusions for her congenital disorder, 11-year-old Dang Thanh Mai Thu is now recovering from a life-saving bone marrow transplant.

Tanvi was diagnosed with thalassemia at just six months. Born into a family facing daily financial struggles, Tanvi’s road to better health has been challenging: her father, Bhupinder Shantilal ...

The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent beta-thalassemia in August 2022, and exagamglogene autotemcel (exa-cel ...

Los Angeles mysterious help sign: Officials are yet to comment on the images, but several theories have sprung up on X. A Los Angeles region near a shipping port has shot into the limelight after ...

The newest gene therapy treatment, Casgevy, treats sick cell disease and transfusion-dependent beta thalassemia. Its addition means that CHLA provides the most cell and gene therapy treatments for ...